SOME of the manifestations of acute intermittent porphyria are suggestive of thyrotoxicosis. These include emotional lability, tachycardia and muscular weakness, and such findings have on occasion led ...

Your urine's colour offers vital health clues, from pale yellow indicating good hydration to darker shades suggesting dehydration. Unusual hues like r ...

Disc Medicine has charted a route to market for bitopertin, its drug candidate for rare disease erythropoietic protoporphyria (EPP), after meeting with the FDA. Shares in the company gained almost 24% ...

Skin photosensitivity is defined as the cutaneous response to UV radiation (UVR) and/or visible light (VL). The Fitzpatrick Skin ...

Congenital erythropoietic porphyria (CEP) or Günther’s disease is an inborn error of heme biosynthesis transmitted as an autosomal recessive trait and ...

Ancient stories have captivated humanity for thousands of years, filled with magical creatures, lost cities, and legendary ...

The CNPV has an expedited review process of 1 to 2 months. According to the FDA, the "cornerstone" of the process is a 1-day ...

Learn more about whether Alnylam Pharmaceuticals, Inc. or Avidity Biosciences, Inc. is a better investment based on AAII's A+ Investor grades, which compare both companies' key financial metrics.

Ionis Pharmaceuticals, Inc. shows promise with new drug launches and a robust pipeline. Click here to read IONS stock ...

The FDA has named six new additions to the Commissioner’s National Priority Voucher (CNPV) program, expanding the initiative to 15 products that address critical public health and national security ...

Eli Lilly will submit orforglipron to be part of FDA’s new national priority voucher program, according to a new report. 1 The company believes it to be a strong candidate for the program.