A year ago, NBC News joined Wedam Minyila as he began undergoing a groundbreaking treatment for sickle cell disease. The ...

A new CRISPR breakthrough shows scientists can turn genes back on without cutting DNA, by removing chemical tags that act ...

Victoria Gray spent 34 years battling the debilitating pain of sickle cell disease. Then she volunteered to be the world's first "prototype" for a CRISPR therapy, based on technology invented at UC ...

A new CRISPR approach can control genes without cutting DNA, opening a safer path for treating genetic diseases. A newly ...

At age 45, Dr. Lakiea Bailey said, for the longest time, that she was the oldest person with sickle cell anemia that she knew. The executive director of the nonprofit patient advocacy group the Sickle ...

The U.S. Food and Drug Administration (FDA) on Friday announced that it has approved Casgevy, the first CRISPR gene-editing therapy for sickle cell disease, paving the way for thousands of patients in ...

Evelyn Quartey carries the sickle cell trait, as did her ex-husband and first son, Emmanuel, who passed away from Sickle Cell Disease in 2009 at 7. Her younger son Gerald had been diagnosed with the ...

LOS ANGELES (KABC) -- It's been more than a month since the FDA approved two milestone gene-editing treatments for sickle cell disease, but lining up patients for these therapies will be a challenge ...

The first study assessing the real-world commercial roll-out of gene therapies for sickle cell disease and beta thalassemia offers lessons learned to inform best practices as manufacturers and medical ...

Expected rapid advances in CAR T and other cellular therapies may expand treatment options not only in cancer but also in ...

Sickle cell anemia is the world's most common genetic disorder. It causes the red blood pigment hemoglobin to crystallize, ...

Scientists already know that people with sickle cell traitare less likely to develop severe malaria. What has never been clear is whythis protection exists.One long-standing idea was that mosquitoes ...