The ability to correct disease-causing genetic mistakes using genome editors holds great promise in medicine, but it is not ...

The approval makes donidalorsen the only treatment in the US for hereditary angioedema that is an RNA-targeted prophylactic.

On Thursday, the U.S. Food and Drug Administration (FDA) approved Ionis Pharmaceuticals, Inc.’s (NASDAQ:IONS) Dawnzera ...

As aging progresses, the quality of DNA and proteins inside cells declines, which is known to be the cause of various ...

Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) announced today that the U.S. Food and Drug Administration (FDA) has approved ...

In the past decade there has been significant interest in studying the expression of our genetic code down to the level of ...

Researchers at San Diego State University and Michigan State University are shedding new light on how viruses meticulously ...

Using artificial intelligence, MIT researchers have come up with a new way to design nanoparticles that can more efficiently ...

Similar to the way the caps on the ends of a shoelace prevent it from fraying, telomeres—regions of repetitive DNA sequences ...

In 1957, just four years after Francis Crick and other scientists solved the riddle of DNA’s structure—the now famous double ...

Since 2008, the FDA has approved 11 treatments for a rare genetic condition called hereditary angioedema (HAE), three of ...

A new nanotube-based RNA delivery system boosts plant regeneration by switching off a molecule that blocks shoot growth, without changing the plant's DNA.