Doctors harvest stem cells from the patient’s bone marrow and then send them off to a lab, where CRISPR is used to turn up the production of another, functional version of haemoglobin. This version is ...
Shortages of Ozempic and Wegovy that have been in place for more than two years have been resolved, as supplies of the ...
"After much consideration, we are postponing FDA-NIH Rare Disease Day 2025 and will reschedule it to occur in the coming months," a notice on the FDA's website showed. Rare Disease Day is observed ...