The ability to correct disease-causing genetic mistakes using genome editors holds great promise in medicine, but it is not ...

Researchers at San Diego State University and Michigan State University are shedding new light on how viruses meticulously ...

The approval makes donidalorsen the only treatment in the US for hereditary angioedema that is an RNA-targeted prophylactic.

The quest for a vaccine against HIV has been going on for about 40 years — almost as long as the virus that causes AIDS has ...

In 1957, just four years after Francis Crick and other scientists solved the riddle of DNA’s structure—the now famous double ...

The ability to correct disease-causing genetic mistakes using genome editors holds great promise in medicine, but it is not ...

Since 2008, the FDA has approved 11 treatments for a rare genetic condition called hereditary angioedema (HAE), three of ...

The collaboration will explore RNA-based small molecule drug candidates aimed at neurological conditions where existing ...

A new study, led by researchers at Children's Hospital of Philadelphia (CHOP), identified tiny pieces of messenger RNA that ...

Developed by Ionis Pharmaceuticals, Dawnzera is the first RNA-targeted medicine approved for HAE, designed to target plasma ...

Senior author Elias Sayour, M.D., Ph.D., a UF Health pediatric oncologist, said the results reveal a potential new treatment path — an alternative to surgery, radiation, and chemotherapy — with broad ...

As aging progresses, the quality of DNA and proteins inside cells declines, known to be the cause of various degenerative ...